Victoria, living with hereditary angioedema
Rare diseases don’t wait. Neither do we.
We develop and deliver therapies for rare immune and genetic diseases.
WHO WE ARE
At Pharming, rare disease breakthroughs aren’t just discovered, they’re created together
We’re built on a simple belief: people living with rare diseases deserve more.
We focus on rare and ultra-rare immunological and genetic diseases, including hereditary angioedema (HAE), activated PI3K delta syndrome (APDS), and primary mitochondrial disease (PMD), all of which require scientific depth and long-term commitment.
Patients are at the heart of our work. We partner closely with the rare disease community, execute with discipline, and reinvest in innovation to strengthen our commercial foundation, expanding access to approved therapies, and advancing focused pipeline programs in areas of clear unmet need.
We deliver today and prepare responsibly for what comes next.
ADVANCING RARE CARE
Where rare diseases meet progress
Every decision begins with patients. In close partnership with the rare disease community, we translate lived experience into focused science, responsible delivery, and measurable progress.
Delivering impact
We design our therapies for real life, prioritizing reliability, quality, and responsible access so patients and families can manage complex conditions with greater confidence. We develop and deliver targeted therapies for people living with rare diseases including HAE and APDS.
Building what comes next
We advance a focused pipeline in rare immune and genetic diseases, targeting the underlying disease drivers of serious rare conditions. We prioritize programs with strong scientific rationale and clear unmet need, investing with discipline to expand treatment options and create long-term impact.
Partnering to accelerate progress
Partnerships are key to how we advance and deliver treatments for rare disease communities. By combining scientific expertise with commercial strength, we turn innovation into new therapies and lasting impact for patients.
“It took me 20 years to receive a diagnosis after countless ER visits and hospitalizations. I was at the end of my rope. Starting a treatment was one of the most incredible moments for me.”
Victoria
Living with hereditary angioedema
“For the first time, I’m not just managing crises—I’m planning for the future.”
Tyler
Living with activated PI3K delta syndrome
LIFE AT PHARMING
We move rare care forward–through people who act with purpose Progress today for a better tomorrow
We’re a team that works with urgency and heart. We roll up our sleeves, challenge assumptions, and stay close to the rare disease community because that’s where real impact begins.
Patients and caregivers aren’t an audience to us; they’re partners who shape our work and push us to go further than medicine alone.
If you thrive on pace, purpose, and ownership, you’ll feel right at home. Here, people come first, curiosity drives progress, and every day is a chance to make a meaningful difference. Curious what it feels like to belong here?
“We are a group of people invested in the impact that we want to have for patients. I feel that is uniquely personal here.”
Leverne
Chief Commercial Officer
“There are patients out there who need us. And we must do everything we can to help them. They don't have time to wait.”
Jim
Executive Director of Sales, U.S.
“We are a group of people invested in the impact that we want to have for patients. I feel that is uniquely personal here.”
Leverne
Chief Commercial Officer
“There are patients out there who need us. And we must do everything we can to help them. They don't have time to wait.”
Jim
Executive Director of Sales, U.S.
Progress in rare diseases happens with patients, not around them
INVESTORS
Clear strategy. Disciplined growth. Long-term value.
Pharming is an integrated biotechnology company with proven capabilities across clinical development, manufacturing, regulatory affairs, and commercialization. We are building a company focused on rare and ultra-rare diseases with approved therapies and an advancing pipeline grounded in scientific rigor, patient insight and real-world need.
Our strategy connects performance with purpose, strengthening our commercial portfolio, investing with discipline, and expanding treatment options for the communities we serve.
OUR NEWS
What’s new at Pharming
Stay up to date with the latest news from Pharming, from clinical and pipeline progress to regulatory milestones, financial results, and company updates as we continue to advance rare disease care.
CAREERS
Join the team
We’re always looking for people who want their work to matter. Interested in using your expertise to help shape the future of rare disease care?